ProQR Strengthens Scientific Advisory Board with Leaders in Inherited Retinal Disease and RNA Therapy

LEIDEN, Netherlands & CAMBRIDGE, Mass., July 21, 2020 (GLOBE NEWSWIRE)

ProQR Therapeutics N.V. (Nasdaq:PRQR), a company dedicated to changing lives through the creation of transformative RNA therapies for severe genetic rare diseases, today announced the strengthening of the Company’s Scientific Advisory Board (SAB) with new members. The SAB members serve as strategic advisors to the Company as it continues to advance its pipeline of RNA therapeutics and its proprietary technology platforms.

“We are strengthening our Scientific Advisory Board with the addition of leading experts in inherited retinal disease and RNA therapies,” said Daniel A. de Boer, Chief Executive Officer of ProQR. “These individuals bring important scientific, medical, and industry experience, as well as diverse perspectives for us to draw upon. I’m excited to work with this distinguished and talented group of advisors and believe their contributions will be significant as we continue advancing our platform for patients living with Inherited Retinal Diseases.”

ProQR’s SAB is comprised of:

• James Shannon, MD, Chair of the SAB, has served on ProQR’s Supervisory Board since 2016. Most recently he was Chief Medical Officer at GlaxoSmithKline until his retirement in 2015.
• Mike Cheetham, PhD, is a Professor of Molecular Cell Biology at the University College London Institute of Ophthalmology. The research in the Cheetham lab is focused on understanding the molecular basis of inherited retinal diseases, developing therapies and the development of 3D retinal organoids.
• Thaddeus (Ted) Drija, MD is the former Global Head of Ophthalmology Research at Novartis. He is Professor of Ophthalmology at Harvard Medical School and an Associate Director of Eye Pathology at the Massachusetts Eye and Ear Infirmary.
• Donald. S. Fong, MD, MPH, is Chief of Ophthalmology and Director of the Kaiser Permanente Southern California Eye Monitoring Center. He is also Clinical Professor of Ophthalmology at University of California, Los Angeles (UCLA) School of Medicine.
• Art Levin, PhD is the Chief Scientific Officer at Avidity Biosciences and has more than two decades of experience in RNA drug development from discovery through drug registration, including the development and registration of the first and only oligonucleotide medicine in ophthalmology, Vitravene.
• Martin Maier, PhD is Vice President Research at Alnylam Pharmaceuticals where he heads the RNAi Discovery group. Through his position at Alnylam and a prior position at Ionis Pharmaceuticals he has more than 20 years of experience in the RNA field.
• Tim Stout, MD, PhD, MBA is an Inherited Retinal Disease specialist and the Sid W. Richardson Professor and Margarett Root Brown Chair of the Department of Ophthalmology, and Director of the Cullen Eye Institute at Baylor College of Medicine.
• Phil Zamore PhD is a Howard Hughes Medical Institute Investigator, Gretchen Stone Cook Chair of Biomedical Sciences, Professor of Biochemistry and Molecular Pharmacology, and Chair of the RNA Therapeutics Institute at the University of Massachusetts Medical School. He is also a co-founder of Alnylam Pharmaceuticals and Voyager Therapeutics.

Biographies for the SAB members are available on ProQR’s website.

About ProQR

ProQR Therapeutics is dedicated to changing lives through the creation of transformative RNA therapies for the treatment of severe genetic rare diseases such as Leber congenital amaurosis 10, Usher syndrome and retinitis pigmentosa. Based on our unique proprietary RNA repair platform technologies we are growing our pipeline with patients and loved ones in mind.

*Since 2012*

FORWARD-LOOKING STATEMENTS

This press release contains forward-looking statements. All statements other than statements of historical fact are forward-looking statements, which are often indicated by terms such as "anticipate," "believe," "could," "estimate," "expect," "goal," "intend," "look forward to", "may," "plan," "potential," "predict," "project," "should," "will," "would" and similar expressions. Such statements include, but are not limited to, statements regarding our SAB members, and statements regarding our ongoing and planned discovery and development of our pipeline and the advancement of our novel and proprietary technologies. Forward-looking statements are based on management's beliefs and assumptions and on information available to management only as of the date of this press release. Our actual results could differ materially from those anticipated in these forward-looking statements for many reasons, including, without limitation, the risks, uncertainties and other factors in our filings made with the Securities and Exchange Commission, including certain sections of our annual report filed on Form 20-F. Given these risks, uncertainties and other factors, you should not place undue reliance on these forward-looking statements, and we assume no obligation to update these forward-looking statements, even if new information becomes available in the future, except as required by law.

ProQR Therapeutics N.V.

Investor Contact:

Sarah Kiely

ProQR Therapeutics N.V.

T: +1 617 599 6228

skiely@proqr.com

or

Hans Vitzthum

LifeSci Advisors

T: +1 617 535 7743

hans@lifesciadvisors.com

Media Contact:

Sara Zelkovic

LifeSci Public Relations

T: +1 646 876 4933

sara@lifescipublicrelations.com